James BazánmRNA shows (showed?) potential for a treatment of Cystic Fibrosis that does not affect a person’s DNA or CFTR mutations. Unlike gene editing or integrating gene therapy, there is no risk of disrupting a person's genome.
The Cystic Fibrosis Foundation does not rely on government funding, but most research partners do.
Keep the fight alive: https://nclvm.com/6abct
David Mitchell :CApride:@JamesBazan@mastodon.coffee
When I was a child around 1980, my mother was camp nurse at an Easter Seals camp for ‘disabled children’, so I attended a cystic fibrosis camp despite not having the disease.
At the time, life expectancy with CF was under 20, and for two weeks the regimen that allowed even that was part of my day. As I moved through high school and into young adulthood it was a sadness to think that those kids had probably all died.
But then I got caught up on the effectiveness of treatments being pioneered and realized that thanks to research supported by the Cystic Fibrosis Foundation life expectancy had been slowly extended to the point that most of my cabin-mates are probably still alive today.
I encourage everyone to support the organization as you are able, and stop helping to elect awful ignorant numpties who value their ideologies ahead of the lives of sick children.
#CysticFibrosis #mRNA